Advancing Research:
The SMA Drug Pipeline
-We now have 13 new SMA drug programs in development, including 3 clinical trials.
-This pipeline has expanded from just 4 programs 5 years ago.
-Families of SMA has funded half of all the ongoing drug programs for SMA.
Supporting Families:
The FSMA Equipment Pool
-In the last year Families of SMA provided direct services to over 3,600 patients and families.
-We supply critical resources specially designed for SMA patients to live a healthy and comfortable life.
-Recently added medical equipment ranges from adaptive bathing systems to positioning strollers.
Giving Hope:
The Annual SMA Conference
-1,500 attendees, 3 times as many families and patients as 5 years ago.
-New specialized programs for newly diagnosed families and for professional care providers.
-Participation has grown to 14 companies, including 3 major pharmaceutical partners.
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1 in 40 people, or 8 million Americans, are genetic carriers.
SMA is the #1 genetic killer of infants.
Families of SMA --Research, Support, Hope
